'Will it really work?': Young sickle cell patient among the first to start new gene therapy

Since two gene therapies were approved for sickle cell disease in late 2023, only a handful of patients have started the expensive treatments.

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'Will it really work?': Young sickle cell patient among the first to start new gene therapy

Topics

Related

Gene therapy treatment gives new hope to sickle cell patients

How Gen Z Bosses Really Feel About Working With Their Own Generation

Young cancer patient who inspired millions with viral Nebraska football touchdown dies at 19

Jack Hoffman, young cancer patient and Nebraska football fan, dies

The big menopause swizz: do hormone supplements really work?

'Confirmed': Curry, Cam Newton among those to celebrate no-look Bryce Young touchdown

2024 NFL Young Player Awards: Jayden Daniels, Brock Bowers among top emerging stars

French red wine in sharp decline as tastes change among young drinkers

Baby to fly to Mexico for 'life-changing' stem cell therapy after fundraiser

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